New Zealand SMA Registry
The New Zealand Spinal Muscular Atrophy (SMA) Registry has been developed to collate a participant’s SMA gene sequence and clinical information about their condition. The Registry provides an important enabling tool for clinicians and clinical trial sponsors to quickly identify participants suitable for each study, particularly those therapeutic strategies that target specific genetic defects. Potentially eligible participants will be informed about new trials and studies through the Registry’s clinical network.
Please visit the SMA Registry website for more information, including the consent form.